Our novel platform integrates cutting-edge small molecule screening and advanced assay technologies to accelerate drug discovery for unmet medical needs in RNA repeat disorders.
We focus on rare diseases such as Huntington's disease, leveraging proprietary RNA-targeting approaches to develop transformative medicines that address the root causes of these conditions.
Committed to innovation, RaritasBio, Inc. combines expertise in biopharma research and medicinal chemistry to deliver novel therapeutic solutions for patients with rare and challenging neurodegenerative diseases.